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Gene therapy treatment shows promise for Parkinson's

12 April 2012

Our director of research, Dr Kieran Breen, was interviewed on Sky News at lunchtime today, commenting on their story about Sheila Roy, a lady with Parkinson's who is taking part in a trial of the gene therapy ProSavin.

Read the full story and watch the Sky News clip.

What is ProSavin?

We're currently funding £750,000 worth of cutting-edge gene therapy research in the UK, which we believe could take these treatments to the next level.

Dr Kieran Breen, our director of research

ProSavin is a gene therapy treatment for Parkinson's that is currently in the early stages (Phase I/II) of clinical trials - which means it's currently being tested in a small group of 15 people with the condition.

ProSavin, developed by British company Oxford BioMedica, contains 3 genes essential for making dopamine.

People with Parkinson's don't have enough of the chemical dopamine because nerve cells in their brain have died. Current treatments help to boost dopamine levels inside the brain but can cause significant side effects.

An injection of ProSavin boosts the ability of nerve cells to make their own dopamine.

This may mean that people with Parkinson's could one day reduce their dependence on current drugs that come with significant side effects.

What are the latest results from the trial?

The latest results from the ProSavin trial were released by Oxford BioMedica in December 2011.

So far the therapy seems to be safe, and participants have showed promising improvements in their Parkinson's symptoms.

But these trials are still in their early stages. Longer and larger studies will need to be carried out to prove the treatment is safe and effective before this treatment becomes available to people with Parkinson's.

The promise of gene therapies

Dr Kieran Breen, Director of Research and InnovationOur director of research and innovation, Dr Kieran Breen (pictured right), comments:

"Gene therapies hold great promise for people with Parkinson's in the future, as they could mean an end to the daily regime of drugs that most people with the condition currently face.

"In addition to ProSavin, there are 3 other gene therapy trials underway at the moment.

"So far all the therapies appear to be safe. Now the challenge is to see whether they are more effective than the medications we already have for Parkinson's.

"Parkinson's UK is currently funding £750,000 worth of cutting-edge gene therapy research in the UK, which we believe could take these treatments to the next level."